A PHASE IIA MULTICENTER, OPEN-LABEL, 12-WEEK STUDY TO INVESTIGATE THE PHARMACOKINETICS AND SAFETY AND TO PROVIDE PROOF OF MECHANISM OF ALOGABAT IN CHILDREN AND ADOLESCENTS AGED 5–17 YEARS WITH ANGELMAN SYNDROME (AS) WITH DELETION GENOTYPE
A PHASE IIA MULTICENTER, OPEN-LABEL, 12-WEEK STUDY TO INVESTIGATE THE PHARMACOKINETICS AND SAFETY AND TO PROVIDE PROOF OF MECHANISM OF ALOGABAT IN CHILDREN AND ADOLESCENTS AGED 5–17 YEARS WITH ANGELMAN SYNDROME (AS) WITH DELETION GENOTYPE